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Gene therapy for MPS


The American Society of Gene & Cell Therapy (ASGCT) have developed a series of patient-friendly resources to educate on gene therapy approaches for MPS. Visit their website to find more information about gene therapy for MPS and to see more videos and resources on the subject. Here's a their gene therapy basics video to give you an idea of what to expect.

Gene therapy basics

Gene therapy has been studied for more than 40 years and can help stop or slow the effects of disease on the most basic level of the human body - our genes. And to understand how it works, we’ll start at the basics.

Gene Therapy Basics